Phase
Condition
N/ATreatment
ALXN2350
Clinical Study ID
Ages 18-70 All Genders
Study Summary
Eligibility Criteria
Inclusion
Inclusion Criteria:
Pathogenic or likely pathogenic mutation in BAG3
Medical history of diagnosis of DCM
Stable combination of HF SoC medications
Adequate acoustic windows for echocardiography
Exclusion
Exclusion Criteria:
Presence of antibodies to AAV9
Presence of a pathogenic or likely pathogenic variant in another gene where thatother gene is authoritatively recognized as causal for DCM.
Decompensated HF
Note: Other inclusion and exclusion criteria may apply.
Study Design
Connect with a study center
Research Site
Massa, 54100
ItalyActive - Recruiting
Research Site
Barcelona, 08035
SpainActive - Recruiting
Research Site
Majadahonda, 28222
SpainActive - Recruiting
Research Site
London, SW3 6NP
United KingdomActive - Recruiting
Research Site
Birmingham, Alabama 35233
United StatesActive - Recruiting
Research Site
Boston, Massachusetts 02115
United StatesActive - Recruiting
Research Site
Cincinnati, Ohio 45219
United StatesActive - Recruiting
Research Site
Portland, Oregon 97239-3098
United StatesActive - Recruiting
Research Site
Philadelphia, Pennsylvania 19104
United StatesActive - Recruiting
Research Site
Houston, Texas 77030
United StatesActive - Recruiting

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