Phase
Condition
Holoprosencephaly
Abnormal Blood Vessels (Arteriovenous Malformations)
Birth Defects
Treatment
Placebo
QTORIN 3.9% Rapamycin Anhydrous Gel
Clinical Study ID
Ages > 3 All Genders
Study Summary
Eligibility Criteria
Inclusion
Key Inclusion Criteria:
Participant must be at least 3 years of age at time of consent/assent
Participant must have a clinically confirmed superficial/cutaneous microcysticlymphatic malformation
Exclusion
Key Exclusion Criteria:
Participants who have vascular malformations that interfere with evaluating thetarget microcystic lymphatic malformation
Participants with complicated vascular anomalies with severe systemic symptoms thatrequire systemic therapy
The participant's treatment area is mainly in any wet mucosa or within the orbitalrim
Participants who are pregnant or planning to become pregnant
Study Design
Connect with a study center
Children's Hospital of Orange County
Irvine, California 92612
United StatesSite Not Available
Stanford University
Palo Alto, California 94305
United StatesSite Not Available
Children's Healthcare of Atlanta
Atlanta, Georgia 30342
United StatesSite Not Available
University of Iowa
Iowa City, Iowa 52245
United StatesSite Not Available
Minnesota Clinical Study Center
New Brighton, Minnesota 55112
United StatesSite Not Available
Mayo Clinic
Rochester, Minnesota 55905
United StatesSite Not Available
Vascular Birthmark Institute
New York, New York 10016
United StatesSite Not Available
University of North Carolina
Chapel Hill, North Carolina 27516
United StatesSite Not Available
Cincinnati Children's Hospital
Cincinnati, Ohio 45229
United StatesSite Not Available
Cleveland Clinic
Cleveland, Ohio 44195
United StatesSite Not Available
Penn State Hershey Medical Center
Hershey, Pennsylvania 17033
United StatesSite Not Available
Children's Hospital of Pennsylvania
Philadelphia, Pennsylvania 19104
United StatesSite Not Available
Children's Hospital of Philadelphia
Philadelphia, Pennsylvania 19104
United StatesSite Not Available
Vanderbilt Children's Hospital
Nashville, Tennessee 37232
United StatesSite Not Available
University of Texas, Dell Children's
Austin, Texas 78723
United StatesSite Not Available
Texas Children's Hospital
Houston, Texas 77030
United StatesSite Not Available
University of Utah Health
Salt Lake City, Utah 84113
United StatesSite Not Available

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