Phase
Condition
Myasthenia Gravis (Chronic Weakness)
Muscular Dystrophy
Spinal Muscular Atrophy
Treatment
Nusinersen Sodium Injection
Clinical Study ID
All Genders
Study Summary
Eligibility Criteria
Inclusion
Key Inclusion Criteria:
Currently receiving or about to initiate treatment with commercial Spinraza in thepostmarketing setting
Genetic documentation of 5q-linked SMA
Exclusion
Key Exclusion Criteria:
Hypersensitivity to the active substance or any of the excipients of Spinraza
Ongoing participation or participation within 6 months or 5 half-lives of the agent (whichever is longer) of enrollment in other interventional clinical trials for thetreatment of SMA
Inability to comply with study requirements
NOTE: Other protocol defined Inclusion/Exclusion criteria may apply.
Study Design
Connect with a study center
Pusan Natioanl University Hospital
Busan,
Korea, Republic ofCompleted
Samsung Changwon Hospital
ChangWon,
Korea, Republic ofActive - Recruiting
Chungbuk National University Hospital
Cheongju-si,
Korea, Republic ofActive - Recruiting
Kyungpook National University Hospital
Daegu,
Korea, Republic ofActive - Recruiting
Yeungnam University Hospital
Daegu,
Korea, Republic ofActive - Recruiting
Chungnam National University Hospital
Daejeon,
Korea, Republic ofActive - Recruiting
Chonnam National University Hospital
Gwangju,
Korea, Republic ofActive - Recruiting
Research site
Jeonju, 54907
Korea, Republic ofSite Not Available
Chonbuk National University Hospital
Jeonju-si,
Korea, Republic ofActive - Recruiting
Asan Medical Center
Seoul,
Korea, Republic ofActive - Recruiting
Korea University Guro Hospital
Seoul,
Korea, Republic ofActive - Recruiting
Korea university Anam Hospital
Seoul,
Korea, Republic ofActive - Recruiting
Samsung Medical Center
Seoul,
Korea, Republic ofActive - Recruiting
Seoul Natioanl University Hospital
Seoul,
Korea, Republic ofActive - Recruiting
Severance Hospital
Seoul, 03722
Korea, Republic ofActive - Recruiting
Severance Hospital, Yonsei University Health System
Seoul,
Korea, Republic ofActive - Recruiting
Pusan National University Yangsan Hospital
Yangsan,
Korea, Republic ofActive - Recruiting
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