Phase
Condition
N/ATreatment
N/AClinical Study ID
All Genders
Study Summary
Eligibility Criteria
Inclusion
Inclusion Criteria:
Signed informed consent and assent as applicable (Appendix 1)
A. Males or females with type 1 PD diagnosed locally with plasminogen activitylevels <50% OR B. First degree family members of a person diagnosed with type 1 PD (includes parents, siblings, half-siblings)
All ages included
Available clinical history and treatment for at least 1 year prior to entry exceptfor infants < 1 year of age
Willingness to provide samples for analysis including DNA, plasma etc.
Willingness to participate in prospective follow-up for up to 3 years
Exclusion
Exclusion Criteria:
Previous organ transplant recipient
Any psychiatric disorder, other mental disorder, or any other medical disorder thatimpairs the subject's ability to give informed consent or to comply with therequirements of the study protocol
Refuses to provide informed consent
Special patient populations, including prisoners or, are deemed medically orcognitively unsuitable for research by their treating physician
Inability to obtain a blood sample due to poor or limited venous access
Study Design
Study Description
Connect with a study center
Hospital Britanico Buenos Aires
Buenos Aires, C1280
ArgentinaActive - Recruiting
Murdoch Children's Research Institute, The Royal Children's Hospital
Melbourne, Victoria 3052
AustraliaActive - Recruiting
Medical University of Innsbruck, University Clinic for Pediatrics and Adolescent Medicine
Innsbruck, A-6020
AustriaActive - Recruiting
CHU Sainte-Justine
Montréal, Quebec H3T 1C5
CanadaActive - Recruiting
CHU de Québec Université Laval
Québec, A0121
CanadaActive - Recruiting
University of Saskatchewan
Saskatoon, SK S7N 0W8
CanadaActive - Recruiting
Alexandra Hospital, Athens, Hematology Department
Athens, 11528
GreeceActive - Recruiting
Angelo Bianchi Bonomi Hemophilia and Thrombosis Center,
Milano, 20122
ItalyActive - Recruiting
University Hospital of Padova
Padua, 35100
ItalyActive - Recruiting
Faculty of Medicine, Chiang Mai University
Chiang Mai, 50200
ThailandActive - Recruiting
Dokuz Eylul University pediatric Pulmonology, Allergy and Clinical Immunology
Izmir, Balçova 35330
TurkeyActive - Recruiting
Istanbul University Cerrahpsasa, Cerrahpsasa Medical Faculty Pediatric Hematology and Oncology Department
Istanbul, 34098
TurkeySite Not Available
Istanbul Üniversitesi Onkoloji Enstitüsü
Istanbul, 34093
TurkeyActive - Recruiting
Yuzuncu Yil University Faculty of Medicine Department of Ophthalmology
Van, 65040
TurkeyActive - Recruiting
Rush University Medical Center
Chicago, Illinois 60612
United StatesActive - Recruiting
Indiana Hemophila @Thrombosis Center
Indianapolis, Indiana 46260
United StatesActive - Recruiting
Stony Brook University | Stony Brook Medicine
East Setauket, New York 11733
United StatesActive - Recruiting
Hemophilia Center of Western Pennsylvania
Pittsburgh, Pennsylvania 15213
United StatesActive - Recruiting
Vanderbilt Children's Hematology-Oncology
Nashville, Tennessee 37232
United StatesActive - Recruiting
Cook Children's Medical Center
Fort Worth, Texas 76104
United StatesActive - Recruiting
The University of Texas Health Science Center at Houston
Houston, Texas 77030
United StatesActive - Recruiting
Seattle Children's Hospital
Seattle, Washington 98105-3901
United StatesActive - Recruiting
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