Phase
Condition
Liver Disorders
Pompe Disease
Treatment
N/AClinical Study ID
Ages > 8 All Genders
Study Summary
Eligibility Criteria
Inclusion
Inclusion Criteria:
Patient must have completed protocol AGLU02704 (NCT00158600)
Patient must provide signed, informed consent prior to performing any study-relatedprocedures
Patient (and patient's legal guardian if patient is under 18 years of age) must havethe ability to comply with the clinical protocol
A female patient of childbearing potential must have a negative pregnancy test atBaseline. (note: all female patients of childbearing potential and sexually maturemales must use a medically accepted method of contraception throughout the study.)
Exclusion
Exclusion Criteria:
- The patient has a medical condition, serious intercurrent illness, or otherextenuating circumstance that, in the opinion of the Investigator, would precludetreatment with alglucosidase alfa.
Study Design
Connect with a study center
Westmead,
AustraliaSite Not Available
Calgary, Alberta
CanadaSite Not Available
Sherbrooke, Quebec
CanadaSite Not Available
Paris,
FranceSite Not Available
Rotterdam,
NetherlandsSite Not Available
Anchorage, Alaska
United StatesSite Not Available
Phoenix, Arizona
United StatesSite Not Available
Beverly Hills, California
United StatesSite Not Available
San Diego, California
United StatesSite Not Available
Washington, District of Columbia
United StatesSite Not Available
Coral Springs, Florida
United StatesSite Not Available
Gainesville, Florida
United StatesSite Not Available
Sarasota, Florida
United StatesSite Not Available
Chicago, Illinois
United StatesSite Not Available
Kansas City, Kansas
United StatesSite Not Available
New Orleans, Louisiana
United StatesSite Not Available
Boston, Massachusetts
United StatesSite Not Available
Omaha, Nebraska
United StatesSite Not Available
New York, New York
United StatesSite Not Available
Durham, North Carolina
United StatesSite Not Available
Cincinnati, Ohio
United StatesSite Not Available
Toledo, Ohio
United StatesSite Not Available
Tulsa, Oklahoma
United StatesSite Not Available
Portland, Oregon
United StatesSite Not Available
Philadelphia, Pennsylvania
United StatesSite Not Available
Pittsburgh, Pennsylvania
United StatesSite Not Available
Greenville, South Carolina
United StatesSite Not Available
Dallas, Texas
United StatesSite Not Available
San Antonio, Texas
United StatesSite Not Available
Seattle, Washington
United StatesSite Not Available
Green Bay, Wisconsin
United StatesSite Not Available
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