Found 6 clinical trials
A Study to Evaluate the Effect of Venglustat Tablets on Left Ventricular Mass Index in Male and Female Adult Participants With Fabry Disease (CARAT)
alfa, agalsidase beta, or migalastat) to evaluate the effect of venglustat on left ventricular mass index (LVMI) in adult participants with Fabry disease and left ventricular hypertrophy.
- 0 views
- 17 Jun, 2022
- 4 locations
A Study to Evaluate the Effect of Venglustat Tablets on Left Ventricular Mass Index in Male and Female Adult Participants With Fabry Disease (CARAT)
alfa, agalsidase beta, or migalastat) to evaluate the effect of venglustat on left ventricular mass index (LVMI) in adult participants with Fabry disease and left ventricular hypertrophy.
- 0 views
- 05 Jul, 2022
- 4 locations
MigALastat Therapy Adherence Among FABRY Patients: A Prospective Multicentral Observational Study (MALTA-FABRY)
This study evaluates adherence to the oral chaperone therapy migalastat in patients with Fabry disease.
- 20 views
- 14 Feb, 2022
- 1 location
French Prospective Observational Cohort Study of Patients With Fabry Disease Treated With Migalastat
This is a cohort study to evaluate the effects of migalastat, on long-term safety, effectiveness, and quality of life (QOL) in patients with Fabry disease.
- 0 views
- 25 Jan, 2021
- 14 locations
Impact of MIgalastat TheRApy on CaRdiac Function in patiEnts With Fabry's Cardiomyopathy (MIRACRE-Fabry Trial)
cardiac condition. 20 patients with genetically confirmed Anderson-Fabry disease who have a plan to start Migalastat will undergo 2D strain, diastolic stress echocardiography, LV vortex flow analysis, and
- 0 views
- 23 Oct, 2021
- 1 location
A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
breastfeeding in women and infants exposed to migalastat.
- 0 views
- 05 Mar, 2022
- 1 location