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Found 4 clinical trials
Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy

Duchenne muscular dystrophy (DMD). To participate in the study, patients must have a documented mutation of the DMD gene that is amenable to exon 53 skipping intervention

dmd gene
duchenne muscular dystrophy
  • 08 Jun, 2022
  • 2 locations
  • 17 Sep, 2022
  • 5 locations
Molecular Analysis of Patients With Neuromuscular Disease

The purpose of this study is to identify genes and proteins responsible for neuromuscular disorders by studying genetic material from individuals with neuromuscular disease, as well as their family members. We are interested in recruiting many types of neuromuscular disease including; Duchenne muscular dystrophy (DMD), Becker muscular dystrophy (BMD), and …

neuromuscular diseases
muscle disorders
muscle biopsy
muscular dystrophy
becker muscular dystrophy
  • 23 Jan, 2022
  • 1 location
Brain INvolvement in Dystrophinopathies (BIND): Deep Functional Phenotyping of Duchenne Muscular Dystrophy and Becker Muscular Dystrophy Patients (WP5 and WP6) Part 2: a Neurobehavioural and MRI Study

The objective of this study is to understand the relationship between DMD and BMD brain comorbidities, and the location of the gene mutation which causes the disease.

Accepts healthy volunteers
  • 20 Sep, 2022
  • 4 locations