I am/have/had
I am looking for
Advanced Filters
Found 2 clinical trials
Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3 (LEAP2MONO)
This is a parallel arm, Phase 3, double-blind, double-dummy, active-comparator, 2 arm study to evaluate the efficacy and safety of daily oral venglustat versus intravenous Cerezyme infusions
neuronopathic gaucher disease
deficiency
replacement therapy
bone pain
platelet count
- 6 views
- 13 May, 2022
- 1 location
Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3 (LEAP2MONO)
This is a parallel arm, Phase 3, double-blind, double-dummy, active-comparator, 2 arm study to evaluate the efficacy and safety of daily oral venglustat versus intravenous Cerezyme infusions
neuronopathic gaucher disease
deficiency
replacement therapy
platelet count
bone pain
- 0 views
- 09 May, 2022
- 1 location