Hunter Syndrome (MPS II) Clinical Trials
A listing of Hunter Syndrome (MPS II) medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.
The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the progression of the rare neurodegenerative disorders and the effects of interventions.
- 359 views
- 26 Jan, 2021
- 1 location
This is an observational study planned to document prospectively disease manifestation and neurocognitive course in pediatric patients with a clinical presentation consistent with neuronopathic ("severe") MPS II undergoing current standard of care and/or intrathecal Elaprase for their condition. Some patients may be offered the opportunity to screen for a gene …
- 0 views
- 15 Aug, 2021
- 4 locations