Pompe Disease Clinical Trials

A listing of Pompe Disease medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.

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Found 140 clinical trials
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Rare disease registries for certain lysosomal storage disorders, including, but not limited to, Fabry, Gaucher, MPS I, and Pompe diseases (each, a Registry)

Rare disease registries for certain lysosomal storage disorders, including, but not limited to, Fabry, Gaucher, MPS I, and Pompe diseases (each, a Registry)

  • 584 views
  • 23 Nov, 2020
  • 1 location
featured
A Phase 3 Multicenter, Randomized, Double Masked, Sham- Controlled Clinical Trial to Assess the Safety and Efficacy of Intravitreal Administration of Zimura (Complement C5 Inhibitor) in Patients With Geographic Atrophy Secondary to Age-Related Macular Degeneration

The objectives of this study are to evaluate the safety and efficacy of Zimura intravitreal administration in patients with geographic atrophy secondary to age-related macular degeneration (AMD

  • 0 views
  • 24 Jun, 2021
  • 1 location
Double-Masked Study of Photrex (Rostaporfin) Photodynamic Therapy in the Treatment of Age-Related Macular Degeneration

neovascularization (CNV) associated with age-related macular degeneration (AMD).

angiography
fluorescein angiography
photodynamic therapy
age-related macular degeneration
neovascularization
  • 38 views
  • 07 Nov, 2020
  • 1 location
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

The purpose of this study is to evaluate the safety, tolerability, and efficacy of a single intravenous infusion of SPK-3006 in adults with clinically moderate, late-onset Pompe disease

replacement therapy
gene therapy
  • 26 views
  • 25 Jul, 2021
  • 21 locations
Treatment of Patients With Neovascular AMD Using Indocyanine Green-Mediated Photothrombosis (i-MP).

To establish the safety and efficacy of indocyanine green-mediated photothrombosis (i-MP) for the treatment of patients with neovascular age-related macular degeneration.

indocyanine green
angiography
fluorescein angiography
drusen
age-related macular degeneration
  • 22 views
  • 07 Nov, 2020
  • 1 location
Intravitreal Bevacizumab Combined With PDT Versus Bevacizumab to Treat Exudative AMD

The purpose of this study is to determine the association of bevacizumab and PDT is safety and effective in the treatment of exudative AMD

bevacizumab
neovascularization
corrected visual acuity
  • 10 views
  • 07 Nov, 2020
  • 1 location
Sub-threshold Micro-Pulse Laser Therapy for Drusen of Dry AMD

To investigate the efficacy and safety of sub-threshold micro-pulse laser therapy for drusen of dry age-related macular degeneration (AMD) .

  • 0 views
  • 08 Mar, 2021
  • 1 location
Phase I Study to Compare CMAB818 Injection and Lucentis in Patients With Wet AMD

This is a randomized, double-blind, two-group parallel, positive-controlled clinical Phase I trial comparing the safety, pharmacokinetics, pharmacodynamics and efficacy of CMAB818 and Lucentis in patients with wet age-related macular degeneration.

  • 0 views
  • 18 Jun, 2021
  • 4 locations
Treat-and-extend Using Aflibercept for Type 3 Neovascularization

Type 3 neovascularization is a subtype of neovascular age-related macular degeneration (AMD) that is characterized by intraretinal neovascularization. Treat-and-extend (TAE) regimen is a widely

  • 0 views
  • 04 Mar, 2021
  • 1 location
Study of Treatment Effects of Combination Therapy of Lucentis Plus Reduced Fluence PDT With Visudyne in Patients With Exudative AMD

The purpose of this study is to determine the benefits, if any, of combination therapy with Lucentis plus reduced fluence photodynamic therapy with Visudyne.

atrophy
vegf
visudyne
vascular endothelial growth factor
bevacizumab
  • 27 views
  • 07 Nov, 2020
  • 1 location