Hemophilia Clinical Trials

A listing of Hemophilia medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.

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Found 17 clinical trials
A Research Study Investigating Mim8 in People With Haemophilia A

perform a second part of the study with patients who suffer from a bleeding disorder called haemophilia A. Haemophilia A is an inherited condition caused by a lack of a protein called factor VIII. Mim8

blood test
  • 21 Jul, 2021
  • 28 locations
Study to Evaluate the Efficacy and Safety of Valoctocogene Roxaparvovec With Prophylactic Steroids in Hemophilia A

This Phase III clinical study will evaluate the safety and effectiveness of valoctocogene roxaparvovec in combination with prophylactic corticosteroids in patients with severe hemophilia A.

  • 24 Jul, 2021
  • 11 locations
Safety Efficacy and PK of BIVV001 in Pediatric Patients With Hemophilia A

Primary Objective: To evaluate the safety of BIVV001 in previously treated pediatric subjects with hemophilia A Secondary Objectives: To evaluate the

  • 24 Jul, 2021
  • 31 locations
Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B

Primary Objective: To confirm appropriate dose levels of fitusiran when administered to male pediatric participants (ages 1 to <12 years of age) with severe hemophilia A or B

bethesda assay
severe haemophilia a
antihemophilic factor
factor ix
  • 28 Jul, 2021
  • 11 locations
Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults

Therapy) in adult male participants with moderately severe or severe hemophilia A (FVIII:C1%) for the study duration of 5 years. The study will enroll eligible participants who have been followed on

factor viii activity
antihemophilic factor
severe haemophilia a
  • 31 Jul, 2021
  • 29 locations
Six Month lead-in Study to Evaluate Prospective Efficacy and Safety Data of Current FIX Prophylaxis Replacement Therapy in Adult Hemophilia B Subjects (FIX:C 2%) or Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Subjects (FVIII:C 1%)

hemophilia A subjects, who are negative for nAb to SB-525 capsid (AAV6), prior to the Phase 3 gene therapy study. The enrollment for hemophilia A participants is completed. At this time participants

antihemophilic factor
gene therapy
severe haemophilia a
Factor VIII
  • 28 Jul, 2021
  • 89 locations
Research Study to Look at How Well the Drug Concizumab Works in Your Body if You Have Haemophilia Without Inhibitors

This study will test how well a new medicine called concizumab works in the body of people with haemophilia A or B without inhibitors. The purpose is to show that concizumab can prevent bleeds

  • 27 Jul, 2021
  • 105 locations
Safety Tolerability and Efficacy Study of Valoctocogene Roxaparvovec in Hemophilia A With Active or Prior Inhibitors

This Phase I/II clinical study will evaluate the safety and efficacy of valoctocogene roxaparvovec in patients with severe haemophilia A and inhibitors to FVIII. Part A of the study will involve

  • 19 Jul, 2021
  • 2 locations
A Post Approval Commitment Study to Gain More Information on How Safe and Effective KOVALTRY is in Chinese Children Adolescents /Adults With Severe Hemophilia A

The goal of this study is to gather more information on safety and efficacy of Kovaltry for the prevention and treatment of bleeds in Chinese children, adolescents/adults with severe hemophilia

  • 20 Jul, 2021
  • 12 locations
A Study to Evaluate the Pharmacokinetics Safety and Tolerability of PEG Recombinant Human Coagulation Factor VIII-Fc Fusion Protein for Injection

patients with severe hemophilia A. The secondary objectives are to monitor anti-durg antibodies and anti-PEG antibodies levels in patients with severe hemophilia A

  • 26 Jul, 2021
  • 4 locations