Pompe Disease Clinical Trials

A listing of Pompe Disease medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.

Filter By
Clear all Advanced
I am/have/had
added new label for I am/have/had
I am looking for
added new label for I am looking for
Advanced Filters
Found 125 clinical trials
PRIMA US-Feasibility Study in Atrophic Dry AMD (PRIMA-FS-US)

In this early feasibility trial the safety and performance of the new retinal prothesis PRIMA is tested in five subjects suffering from atrophic dry age related macular degeneration.

  • 20 Jun, 2022
  • 3 locations
Episcleral Brachytherapy for the Treatment of Wet AMD (NEAMES)

This is a prospective, multi-site, safety and feasibility study of the SalutarisMD SMD-DA system for retrobulbar minimally invasive episcleral brachytherapy device in patients receiving and not responding to anti-VEGF therapy for nAMD. The trial will be open label and non-randomized. The study intervention is a one-time intervention and requires no …

  • 26 Mar, 2022
  • 2 locations
Multicenter Clinical Study of the SING-IMT in Patients With Late-stage AMD (CONCERTO)

central vision loss due to late-stage age-related macular degeneration (AMD).

  • 15 Jul, 2022
  • 2 locations
Survival of Monocytes Collected From Patients With Atrophic AMD in Retinal Pigmented Epithelium Explants (SURViVOR)

Age-related macular degeneration (AMD) affects 2 million people in France and is the main cause of irreversible blindness in France. All patients initially have an early form of the disease

retinal pigment
  • 03 Jul, 2022
  • 1 location
RGX-314 Gene Therapy Administered in the Suprachoroidal Space for Participants With Neovascular Age-Related Macular Degeneration (nAMD) (AAVIATE)

RGX-314 is being developed as a novel one-time gene therapy treatment for the treatment of neovascular (wet) age related macular degeneration (wet AMD). Wet AMD is characterized by loss of

  • 20 Apr, 2022
  • 15 locations
Impact of Regular Consumption of Grapes on Eye Health in Singapore Older Adults

Aging epidemics in Singapore are rapidly increasing and Age-related macular degeneration (AMD) prevalence is significantly associated with older age. This study aims to understand the effect of

Accepts healthy volunteers
  • 27 Apr, 2022
  • 1 location
FocuS: First in Human Study to Evaluate the Safety and Efficacy of GT005 Administered in Subjects With Dry AMD

This is an open label first in human Phase I/II multicentre study of GT005 in subjects with Macular Atrophy due to AMD

fundus autofluorescence imaging
fundus photography
macular atrophy
  • 12 Feb, 2022
  • 6 locations
The Role of Complement Factor H Polymorphism in the Regulation of Choroidal Vascular Tone in Young Healthy Subjects

Age related macular degeneration (AMD) is a multifactorial disease with a strong genetic component. Given that it is known that impaired regulation of choroidal vascular tone is present in

age-related macular degeneration
flashing lights
macular pigment
Accepts healthy volunteers
  • 20 Apr, 2022
  • 1 location
The Implementation of Educational Interventions on the Prescribing of Antimicrobial Drugs in Primary Health Care

World increase in mortality from consequences of antimicrobial resistance (AMR) represents a significant public health problem. Irrational prescribing of antimicrobial drugs (AMD) in general

Accepts healthy volunteers
  • 09 Nov, 2021
  • 1 location
Vitrectomy, Subretinal Tissue Plasminogen Activator (TPA) and Intravitreal Gas for Submacular Haemorrhage Secondary to Exudative (Wet) Age-related Macular Degeneration (TIGER). (TIGER)

called wet age-related macular degeneration (AMD), where new abnormal blood vessels grow through the macula and leak fluid. This can affect vision. In some cases, wet AMD can also cause a bleed under the

  • 11 Aug, 2022
  • 14 locations