Gaucher Disease Clinical Trials

A listing of Gaucher Disease medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.

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Found 8 clinical trials
  • 6 views
  • 29 Sep, 2022
  • 1 location
  • 0 views
  • 14 Sep, 2022
  • 4 locations
A Phase 1/2, Open-label, Safety, Tolerability, and Efficacy Study of FLT201 in Adult Patients With Gaucher Disease Type 1 (GALILEO-1) (GALILEO-1)

This study is a first-in-human, phase 1/2, open-label, safety, tolerability, and efficacy study in adult patients with Gaucher disease Type 1. The aims are to investigate the safety/tolerability

  • 0 views
  • 14 Sep, 2022
  • 1 location
Gaucher Disease Registry Protocol

The ICGG Gaucher Registry is an ongoing, international multi-center, strictly observational program that tracks the routine clinical outcomes for patients with Gaucher disease, irrespective of

type 1 gaucher disease
alglucerase
deficiency
imiglucerase
eliglustat
  • 522 views
  • 14 Sep, 2022
  • 207 locations
Gaucher Disease Registry Protocol

The ICGG Gaucher Registry is an ongoing, international multi-center, strictly observational program that tracks the routine clinical outcomes for patients with Gaucher disease, irrespective of

type 1 gaucher disease
alglucerase
deficiency
imiglucerase
eliglustat
  • 0 views
  • 09 Sep, 2022
  • 286 locations
Drug Discovery for Parkinson's With Mutations in the GBA Gene

The New York Stem Cell Foundation (NYSCF) is performing this research to accelerate Parkinson's disease research and drug development by using cells from the body (such as skin or blood cells) to make stem cells and other types of cells, conduct research on the samples, perform genetic testing, and/or store …

parkinson's disease
gba gene
Accepts healthy volunteers
  • 0 views
  • 19 Sep, 2022
  • 1 location
An Observational National Pediatric Study on Prevalence of Unexplained Splenomegaly (OPPUS)

Primary Objective: To assess prevalence of Gaucher disease (GD) diagnosed in pediatric patients presenting with unexplained splenomegaly (SMG) after exclusion of first intention-diagnoses

  • 0 views
  • 14 Sep, 2022
  • 38 locations
Natural History of Glycosphingolipid Storage Disorders and Glycoprotein Disorders

treatment. Patients of any age with Tay-Sachs disease, Sandhoff disease, GM1 gangliosidosis, or type 2 Gaucher disease may be eligible for this study. Participants will be admitted to the NIH

MRI
deficiency
  • 76 views
  • 19 Sep, 2022
  • 1 location