A US Non-interventional, Effectiveness and Safety Study of Patients Treated With SKYTROFA

Last updated: May 1, 2025
Sponsor: Ascendis Pharma Endocrinology Division A/S
Overall Status: Active - Recruiting

Phase

N/A

Condition

Hormone Deficiencies

Severe Short Stature

Treatment

No intervention

Clinical Study ID

NCT05820672
ASND0037
  • Ages 1-18
  • All Genders

Study Summary

The goal of this study is to genrate evidence on long-term effectiveness and safety of SKYTROFA (lonapegsomatropin) in patients with growth hormone deficiency under routine clinical care

Eligibility Criteria

Inclusion

Inclusion Criteria:

  • Patients who are on treatment with SKYTROFA (lonapegsomatropin)

  • Patients being clinically managed in USA

  • Patients with an appropriate written informed consent/assent as applicable for theage of the patient

Exclusion

Exclusion Criteria:

  • Patients participating in any interventional clinical study

Study Design

Total Participants: 900
Treatment Group(s): 1
Primary Treatment: No intervention
Phase:
Study Start date:
March 20, 2023
Estimated Completion Date:
March 31, 2033

Study Description

Patients will be treated according to routine clinical practice, and no additional visits, examinations or tests will be required beyond those performed as part of routine clinical practice except for COAs.

Connect with a study center

  • Ascendis Investigational Site

    Phoenix, Arizona 85054
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Sacramento, California 95821
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    San Francisco, California 94143
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Centennial, Colorado 09582
    United States

    Active - Recruiting

  • Ascendis Pharma Investigational Site

    Centennial, Colorado 80112
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Washington, District of Columbia 20010
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Orlando, Florida 32827
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Tampa, Florida 33612
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Sandy Springs, Georgia 30350
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Boise, Idaho 83712
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Indianapolis, Indiana 46202
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Iowa City, Iowa 52242
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Louisville, Kentucky 40202
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Minneapolis, Minnesota 55455
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Las Vegas, Nevada 89113
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Lebanon, New Hampshire 03756
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Morristown, New Jersey 07960
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    New Brunswick, New Jersey 08901
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    New Hyde Park, New York 11042
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Portland, Oregon 97239
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Columbia, South Carolina 29203
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    El Paso, Texas 79938
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Norfolk, Virginia 23505
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Seattle, Washington 98105
    United States

    Active - Recruiting

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