A US Non-interventional, Effectiveness and Safety Study of Patients Treated With SKYTROFA

Last updated: October 24, 2025
Sponsor: Ascendis Pharma Endocrinology Division A/S
Overall Status: Active - Recruiting

Phase

N/A

Condition

Hormone Deficiencies

Growth Hormone Deficiencies/abnormalities

Severe Short Stature

Treatment

No intervention

Clinical Study ID

NCT05820672
ASND0037
  • Ages 1-18
  • All Genders

Study Summary

The goal of this study is to genrate evidence on long-term effectiveness and safety of SKYTROFA (lonapegsomatropin) in patients with growth hormone deficiency under routine clinical care

Eligibility Criteria

Inclusion

Inclusion Criteria:

  • Patients who are on treatment with SKYTROFA (lonapegsomatropin)

  • Patients being clinically managed in USA

  • Patients with an appropriate written informed consent/assent as applicable for theage of the patient

Exclusion

Exclusion Criteria:

  • Patients participating in any interventional clinical study

Study Design

Total Participants: 900
Treatment Group(s): 1
Primary Treatment: No intervention
Phase:
Study Start date:
March 20, 2023
Estimated Completion Date:
March 31, 2033

Study Description

Patients will be treated according to routine clinical practice, and no additional visits, examinations or tests will be required beyond those performed as part of routine clinical practice except for COAs.

Connect with a study center

  • Ascendis Investigational Site

    Phoenix, Arizona 85054
    United States

    Site Not Available

  • Ascendis Investigational Site

    Phoenix 5308655, Arizona 5551752 85054
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Sacramento, California 95821
    United States

    Site Not Available

  • Ascendis Investigational Site

    San Francisco, California 94143
    United States

    Site Not Available

  • Ascendis Investigational Site

    Sacramento 5389489, California 5332921 95821
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    San Francisco 5391959, California 5332921 94143
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Centennial, Colorado 09582
    United States

    Site Not Available

  • Ascendis Pharma Investigational Site

    Centennial, Colorado 80112
    United States

    Active - Recruiting

  • Ascendis Pharma Investigational Site

    Centennial 5416541, Colorado 5417618 80112
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Washington, District of Columbia 20010
    United States

    Site Not Available

  • Ascendis Investigational Site

    Washington D.C. 4140963, District of Columbia 4138106 20010
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Orlando, Florida 32806
    United States

    Site Not Available

  • Ascendis Investigational Site

    Tampa, Florida 33612
    United States

    Site Not Available

  • Ascendis Investigational Site

    Orlando 4167147, Florida 4155751 32806
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Tampa 4174757, Florida 4155751 33612
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Sandy Springs, Georgia 30350
    United States

    Site Not Available

  • Ascendis Investigational Site

    Sandy Springs 4221333, Georgia 4197000 30350
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Boise, Idaho 83712
    United States

    Site Not Available

  • Ascendis Investigational Site

    Boise 5586437, Idaho 5596512 83712
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Indianapolis, Indiana 46202
    United States

    Site Not Available

  • Ascendis Investigational Site

    Indianapolis 4259418, Indiana 4921868 46202
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Iowa City, Iowa 52242
    United States

    Site Not Available

  • Ascendis Investigational Site

    Iowa City 4862034, Iowa 4862182 52242
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Louisville, Kentucky 40202
    United States

    Site Not Available

  • Ascendis Investigational Site

    Louisville 4299276, Kentucky 6254925 40202
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Minneapolis, Minnesota 55455
    United States

    Site Not Available

  • Ascendis Investigational Site

    Minneapolis 5037649, Minnesota 5037779 55455
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Las Vegas, Nevada 89113
    United States

    Site Not Available

  • Ascendis Investigational Site

    Las Vegas 5506956, Nevada 5509151 89113
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Lebanon, New Hampshire 03756
    United States

    Site Not Available

  • Ascendis Investigational Site

    Lebanon 5088597, New Hampshire 5090174 03756
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Morristown, New Jersey 07960
    United States

    Site Not Available

  • Ascendis Investigational Site

    New Brunswick, New Jersey 08901
    United States

    Site Not Available

  • Ascendis Investigational Site

    Morristown 5101427, New Jersey 5101760 07960
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    New Brunswick 5101717, New Jersey 5101760 08901
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    New Hyde Park, New York 11042
    United States

    Site Not Available

  • Ascendis Investigational Site

    New Hyde Park 5128514, New York 5128638 11042
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Portland, Oregon 97239
    United States

    Site Not Available

  • Ascendis Investigational Site

    Portland 5746545, Oregon 5744337 97239
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Columbia, South Carolina 29203
    United States

    Site Not Available

  • Ascendis Investigational Site

    Columbia 4575352, South Carolina 4597040 29203
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    El Paso, Texas 79938
    United States

    Site Not Available

  • Ascendis Investigational Site

    El Paso 5520993, Texas 4736286 79938
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Norfolk, Virginia 23505
    United States

    Site Not Available

  • Ascendis Investigational Site

    Norfolk 4776222, Virginia 6254928 23505
    United States

    Active - Recruiting

  • Ascendis Investigational Site

    Seattle, Washington 98105
    United States

    Site Not Available

  • Ascendis Investigational Site

    Seattle 5809844, Washington 5815135 98105
    United States

    Active - Recruiting

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