A Prospective Study Evaluating Seroprevalence and Seroconversion of Antibodies Against Adeno-associated Virus (AAV)

Last updated: August 15, 2024
Sponsor: BioMarin Pharmaceutical
Overall Status: Terminated

Phase

N/A

Condition

Hemophilia

Treatment

Biospecimen Collection

Clinical Study ID

NCT05580692
270-702
  • Ages > 18
  • All Genders

Study Summary

A prospective cohort study utilizing biospecimen sample collection from adult Hemophilia A subjects to evaluate and characterize seroprevalence and the seroconversion of antibodies against AAV serotypes

Eligibility Criteria

Inclusion

Inclusion Criteria:

  • Adult Subjects with Hemophilia A

Exclusion

Exclusion Criteria:

  • Subject previously treated with AAV vector gene therapy

Study Design

Total Participants: 321
Treatment Group(s): 1
Primary Treatment: Biospecimen Collection
Phase:
Study Start date:
March 14, 2023
Estimated Completion Date:
July 31, 2024

Study Description

This is a multinational, multi-center, prospective cohort study utilizing biospecimen sample collection from adult Hemophilia A subjects to evaluate and characterize seroprevalence and the seroconversion of antibodies against AAV serotypes

Connect with a study center

  • Instituto Hematologia Arbesu

    Godoy Cruz, Mendoza M5504FKD
    Argentina

    Site Not Available

  • Hospital Ramon Jose Vidal

    Corrientes, W3410 FND
    Argentina

    Site Not Available

  • Medico Hematologo

    Mendoza,
    Argentina

    Site Not Available

  • Instituto de Hematologia y Medicina Clinica Dr. RUben Davoli

    Rosario, S2000 CFK
    Argentina

    Site Not Available

  • Royal Prince Alfred Hospital

    Camperdown, 2050
    Australia

    Site Not Available

  • Haemophilia and Haemostasis Centre Level 1 Cancer Centre South Metropolitan Health Service Fiona Stanley Hospital

    Murdoch, 6150
    Australia

    Site Not Available

  • Medical University of Vienna

    Wien, 1090
    Austria

    Site Not Available

  • King Faisal Specialist Hospital & Research Center

    Riyadh, 11211
    Saudi Arabia

    Site Not Available

  • King Saud University Medical City King Saud University

    Riyadh, 12372
    Saudi Arabia

    Site Not Available

  • Skane University Hospital

    Malmö, 205 02
    Sweden

    Site Not Available

  • ME Centrum för kliniska cancerstudier - House H3

    Solna, SE-171 76
    Sweden

    Site Not Available

  • Acibadem Adana Hospital

    Adana, 01130
    Turkey

    Site Not Available

  • Hacettepe University

    Ankara, 06100
    Turkey

    Site Not Available

  • Gaziantep University Medical Faculty Sahinbey Educational Research Hospital

    Gaziantep, 27310
    Turkey

    Site Not Available

  • Istanbul University Cerrahpasa - Cerrahpasa Medical Faculty

    Istanbul, 34098
    Turkey

    Site Not Available

  • Ondokuz Mayis Univ. Med. Fac.

    Samsun, 55270
    Turkey

    Site Not Available

  • Ege University Medical Faculty

    İzmir, 35040
    Turkey

    Site Not Available

  • Sheikh Shakhbout Medical City

    Abu Dhabi, 11393
    United Arab Emirates

    Site Not Available

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