Phase
Condition
Muscular Dystrophy
Treatment
N/AClinical Study ID
Ages > 4 All Genders
Study Summary
Eligibility Criteria
Inclusion
Inclusion Criteria:
Any of the following are true:
Currently has a confirmed diagnosis of DMD/BMD based on genetic testing, musclebiopsy, or clinical diagnosis.
Currently has a confirmed diagnosis of carrier status for DMD/BMD based ongenetic testing.
Parent/guardian (for minor participants) or participant gives informed consentand/or assent as required by local regulations.
Is age 4 weeks or older at the time of consent.
Exclusion
Exclusion Criteria:
Is a foster child or ward of the state.
Is a prisoner.
Study Design
Study Description
Connect with a study center
Arkansas Children's Hospital
Little Rock, Arkansas 72202
United StatesActive - Recruiting
CureDuchenne
Newport Beach, California 92660
United StatesActive - Recruiting
Children's Hospital of Orange County
Orange, California 92868
United StatesActive - Recruiting
Rare Disease Research
Atlanta, Georgia 30329
United StatesActive - Recruiting
University of Iowa
Iowa City, Iowa 52242
United StatesActive - Recruiting
Kansas University Clinical Research Center
Fairway, Kansas 66205
United StatesActive - Recruiting
Corewell Health
Grand Rapids, Michigan 49503
United StatesActive - Recruiting
Rare Disease Research Center
Hillsborough, North Carolina 27278
United StatesActive - Recruiting
Penn State Health
Hershey, Pennsylvania 17033
United StatesActive - Recruiting
Neurology Rare Disease Center
Denton, Texas 76208
United StatesActive - Recruiting
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