Last updated on January 2020

Safety Pharmacodynamics and Efficacy of Migalastat in Pediatric Subjects (Aged >12 Years) With Fabry Disease

Brief description of study

This is a long-term, Open-label Study to Evaluate the Safety, Pharmacodynamics, and Efficacy of Migalastat in Subjects > 12 Years of Age With Fabry Disease and Amenable GLA Variants

Clinical Study Identifier: NCT04049760

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