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Therapeutic Areas: Pediatrics/Neonatology
Clinical Trials: Pompe Disease
A listing of clinical trials currently looking for volunteers to enroll in Pompe Disease studies. Click on the closest city to find more detailed information on a research study in your area.
Alabama
Birmingham : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Arizona
Phoenix : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Phoenix : Phoenix Neurological Associates, Ltd
Drug-drug Interaction Study
Scottsdale : Neuromuscular Research Center
Drug-drug Interaction Study
Arkansas
Little Rock : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
California
La Jolla : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
La Jolla : Univ of California San Diego School of Medicine Updated
Extension Study for Patients Who Have Completed BMN 701 Studies
La Jolla : Univ of California San Diego School of Medicine Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
Los Angles : UCLA Neurological Services Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
Oakland : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
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Orange : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
San Jose : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Stanford : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Colorado
Aurora : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Florida
Gainesville : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Gainesville : University of Florida College of Medicine Updated
Extension Study for Patients Who Have Completed BMN 701 Studies
Gainesville :
Growth and Development Study of Myozyme (Alglucosidase Alfa).
Gainesville : University of Florida College of Medicine Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
Gainsville : University of Florida, Department of Pediatrics, Powell Gene Therapy Center
Drug-drug Interaction Study
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Miami : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Georgia
Decatur : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Decatur : Emory University
Drug-drug Interaction Study
Decatur :
Growth and Development Study of Myozyme (Alglucosidase Alfa).
Illinois
Chicago : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Indiana
Indianapolis : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Kansas
Kansas City : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Kansas City : University of Kansas Medical Center
Drug-drug Interaction Study
Kansas City : University of Kansas Medical Center Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
Kentucky
Louisville :
Immune Tolerance Induction Study
Louisiana
Baton Rouge : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Shreveport : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Massachusetts
Michigan
Detriot : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Detroit :
Growth and Development Study of Myozyme (Alglucosidase Alfa).
Grand Rapids : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Minnesota
Minneapolis : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Missouri
Columbia : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Kansas City : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
St. Louis : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Montana
Nebraska
Omaha : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
New Jersey
New Brunswick : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
New York
Glenn Falls : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
New York : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Syracuse : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Valhalla : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
North Carolina
Asheville : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Durham : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Durham : Duke University Medical Center
Drug-drug Interaction Study
Durham :
Growth and Development Study of Myozyme (Alglucosidase Alfa).
Durham :
Immune Tolerance Induction Study
Ohio
Cincinnati : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Cleveland : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Pennsylvania
Philadelphia : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Pittsburgh : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Rhode Island
Providence : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Tennessee
Memphis : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Nashville : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Texas
Austin : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Fort Worth : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Utah
Salt Lake City : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Salt Lake City :
Immune Tolerance Induction Study
Virginia
Norfolk : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Norfolk :
Immune Tolerance Induction Study
Springfield : LSD Research and Treatment Center, CFCT
Drug-drug Interaction Study
Washington
Seattle : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
West Virginia
Morgantown : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Wisconsin
Milwaukee : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Australia
Herston : Royal Brisbane and Women's Hospital Updated
Extension Study for Patients Who Have Completed BMN 701 Studies
Canada
France
Nice : Hôpital de I´Archet- Centre Hospitalier Universitaire Nice Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
Paris : Hôpital Pitié-Salpêtrière Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
Israel
Haifa :
Immune Tolerance Induction Study
United Kingdom
Birmingham : University Hospitals Birmingham NHS Foundation Trust Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
London : Royal Free Hospital Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
Salford : Salford Royal Hospital NHS Trust Updated
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
United States
Washington : Updated
A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
