Phase
Condition
Wolman Disease
Polymyositis (Inflammatory Muscle Disease)
Hyponatremia
Treatment
Prednisone/Prednisolone
Ravulizumab
Oral Corticosteroid Tapering Schedule
Clinical Study ID
Ages > 18 All Genders
Study Summary
Eligibility Criteria
Inclusion
Inclusion Criteria:
Aged greater than 18 years and male or female
Clinical diagnosis of gMG
Receiving ravulizumab treatment prior to enrollment
Receipt of OCS therapy equivalent to a daily dose ≥ 7.5 mg ofprednisone/prednisolone for ≥ 4 continuous weeks directly preceding enrollment
A participant of childbearing potential must have a negative highly sensitivepregnancy test (serum or urine, as required by local regulations) taken at Screeningbefore OCS tapering begins.
Willing to sign informed consent
Exclusion
Exclusion Criteria:
Concurrent participation in an interventional clinical trial.
History of chronic hypoadrenalism (ie, Addison's disease).
Use of concomitant OCS for comorbid conditions other than gMG
Receipt of a biologic for gMG (e.g., efgartigimod, rozanolixizumab, inebilizumab,rituximab, intravenous immunoglobulin) within 5 half-lives of enrollment
Pregnant, breastfeeding, or intending to conceive during the course of the study
Study Design
Connect with a study center
Research Site
Bochum, 44789
GermanySite Not Available
Research Site
Bochum 2947416, 44789
GermanySite Not Available
Research Site
Essen 2928810, 45147
GermanySite Not Available
Research Site
Milan, 20122
ItalySite Not Available
Research Site
Milan 6951411, 20122
ItalySite Not Available
Research Site
Naples, 80131
ItalySite Not Available
Research Site
Napoli, 80131
ItalySite Not Available
Research Site
Napoli 9031661, 80131
ItalySite Not Available
Research Site
Rome, 00189
ItalySite Not Available
Research Site
Rome 3169070, 00189
ItalySite Not Available
Research Site
Ibaraki, 305-8576
JapanSite Not Available
Research Site
Ibaraki 1862033, 305-8576
JapanSite Not Available
Research Site
Kitakyushu-shi, 807-8555
JapanSite Not Available
Research Site
Kumamoto, 860-8556
JapanSite Not Available
Research Site
Kumamoto 1858421, 860-8556
JapanSite Not Available
Research Site
Chicago, Illinois 60637
United StatesSite Not Available
Research Site
Schaumburg, Illinois 60173
United StatesSite Not Available
Research Site
Chicago 4887398, Illinois 4896861 60637
United StatesSite Not Available
Research Site
Schaumburg 4910713, Illinois 4896861 60173
United StatesSite Not Available
Research Site
Neptune City, New Jersey 07753
United StatesSite Not Available
Research Site
Neptune City 5101687, New Jersey 5101760 07753
United StatesSite Not Available
Research Site
Raleigh, North Carolina 27607
United StatesActive - Recruiting
Research Site
Raleigh 4487042, North Carolina 4482348 27607
United StatesSite Not Available
Research Site
Pittsburgh 5206379, Pennsylvania 6254927 15212
United StatesSite Not Available
Research Site
Knoxville, Tennessee 37920
United StatesSite Not Available
Research Site
Chattanooga 4612862, Tennessee 4662168 37403
United StatesSite Not Available
Research Site
Knoxville 4634946, Tennessee 4662168 37920
United StatesSite Not Available

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