Last updated on April 2018

Pilot Study of Metformin for Patients With Fanconi Anemia

Brief description of study

This is a single institution, open-label, single arm pilot study of Metformin in patients with Fanconi Anemia (FA) and cytopenias with the primary endpoint of hematologic response. This study will also assess safety, tolerability, and the biologic effects of Metformin in patients with FA.

Clinical Study Identifier: NCT03398824

Contact Investigators or Research Sites near you

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Akiko Shimamura, MD, PhD

Boston Children's Hospital
Boston, MA United States
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